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Orchard Therapeutics plc

Orchard Therapeutics plc

ORTX
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ORCHARD THERAPEUTICS CELEBRATES ADDITION OF METACHROMATIC LEUKODYSTROPHY TO THE U.S. RECOMMENDED UNIFORM SCREENING PANEL

16-12-2025
NEWBORN SCREENING IS THE ONLY PRACTICAL MEANS OF DIAGNOSING MLD PRIOR TO THE ONSET OF SYMPTOMS, WHIC...

ORCHARD THERAPEUTICS ANNOUNCES LAST PATIENT TREATED IN REGISTRATIONAL TRIAL OF OTL-203 FOR MPS-I HURLER SYNDROME

07-07-2025
COMPLETION OF ENROLLMENT ACHIEVED NEARLY ONE YEAR AHEAD OF SCHEDULE PRIMARY ANALYSIS ANTICIPATED TWO...

ORCHARD THERAPEUTICS ANNOUNCES REIMBURSEMENT AGREEMENT IN SPAIN

28-02-2025
LONDON, MADRID, AND BOSTON, FEB. 28, 2025 (GLOBE NEWSWIRE) --  ORCHARD THERAPEUTICS, A KYOWA KIRIN ...

ORCHARD THERAPEUTICS APPOINTS ROBIN KENSELAAR TO CHIEF COMMERCIAL OFFICER AND ANNOUNCES MULTIPLE BUSINESS UPDATES PERTAINING TO ITS APPROVED HSC GENE THERAPY FOR MLD

12-02-2025
FIRST U.S. PATIENTS BEING TREATED WITH LENMELDY™ (ATIDARSAGENE AUTOTEMCEL) IN A COMMERCIAL SETTING...

ORCHARD THERAPEUTICS ANNOUNCES MULTIPLE DATA PRESENTATIONS AND RECEIVES 2025 NEW TREATMENT AWARD AT THE 21ST ANNUAL WORLDSYMPOSIUM™

03-02-2025
FEATURED DATA SHOWCASE THE TRANSFORMATIVE POTENTIAL OF HSC GENE THERAPY TO ENABLE CROSS-CORRECTION A...

ORCHARD THERAPEUTICS ANNOUNCES MULTIPLE DATA PRESENTATIONS AND PUBLICATIONS

23-10-2024
TEN PRESENTATIONS AT ESGCT 2024 DETAIL THE THERAPEUTIC POTENTIAL AND APPLICABILITY OF THE COMPANY'S ...

ORCHARD THERAPEUTICS AND ER-KIM ANNOUNCE PARTNERSHIP TO BROADEN ACCESS TO LIBMELDY TO ELIGIBLE PATIENTS IN TURKEY AND CERTAIN EURASIAN COUNTRIES

07-10-2024
ISTANBUL AND LONDON, AND BOSTON, OCT. 07, 2024 (GLOBE NEWSWIRE) -- ORCHARD THERAPEUTICS, RECENTLY AC...

ORCHARD THERAPEUTICS ANNOUNCES MULTIPLE PRESENTATIONS FROM ACROSS ITS LATE-STAGE NEUROMETABOLIC PORTFOLIO AT SSIEM 2024

28-08-2024
LONDON AND BOSTON, AUG. 28, 2024 (GLOBE NEWSWIRE) -- ORCHARD THERAPEUTICS, RECENTLY ACQUIRED BY KYOW...

ORCHARD THERAPEUTICS CELEBRATES GLOBAL PROGRESS TOWARD ADVANCING NEWBORN SCREENING FOR MLD ON INTERNATIONAL NEONATAL SCREENING DAY

28-06-2024
A NOMINATION TO ADD MLD TO THE U.S. RECOMMENDED UNIFORM SCREENING PANEL HAS BEEN SUBMITTED BY A MULT...

ORCHARD THERAPEUTICS ANNOUNCES MULTIPLE PRESENTATIONS AT ASGCT 2024

07-05-2024
EIGHT PRESENTATIONS SHOWCASE THE BROAD APPLICABILITY OF HSC GENE THERAPY TO ADDRESS RARE NEUROMETABO...

ORCHARD THERAPEUTICS CO-FOUNDER AND CHIEF EXECUTIVE OFFICER DR. BOBBY GASPAR NAMED TO INAUGURAL 2024 TIME100 HEALTH LIST

03-05-2024
TOKYO, LONDON AND BOSTON, MAY 03, 2024 (GLOBE NEWSWIRE) -- ORCHARD THERAPEUTICS, RECENTLY ACQUIRED B...

ORCHARD THERAPEUTICS OUTLINES U.S. LAUNCH PLANS FOR LENMELDY™ (ATIDARSAGENE AUTOTEMCEL), THE ONLY APPROVED THERAPY FOR CHILDREN WITH EARLY-ONSET METACHROMATIC LEUKODYSTROPHY

20-03-2024
FIVE SPECIALIZED TREATMENT CENTERS BEING QUALIFIED ACROSS THE U.S. TO MINIMIZE TRAVEL BURDEN ON ELIG...

ORCHARD THERAPEUTICS RECEIVES FDA APPROVAL OF LENMELDY™ (ATIDARSAGENE AUTOTEMCEL), THE ONLY THERAPY FOR ELIGIBLE CHILDREN WITH EARLY-ONSET METACHROMATIC LEUKODYSTROPHY IN THE U.S.

18-03-2024
ONE-TIME TREATMENT WITH LENMELDY HAS SHOWN THE POTENTIAL TO RESTORE ENZYMATIC FUNCTION TO STOP OR SL...

ORCHARD THERAPEUTICS ANNOUNCES FIRST PATIENT RANDOMIZED IN REGISTRATIONAL TRIAL OF OTL-203 FOR MPS-I HURLER SYNDROME

05-02-2024
GENE THERAPY BEING DEVELOPED AS A ONE-TIME TREATMENT TO ADDRESS THE UNDERLYING CAUSE OF THE DISEASE ...

ORCHARD THERAPEUTICS ANNOUNCES MULTIPLE PRESENTATIONS AT THE 20TH ANNUAL WORLDSYMPOSIUM

02-02-2024
THREE ORAL PRESENTATIONS AND SEVEN POSTERS HIGHLIGHT TRANSFORMATIVE POTENTIAL OF HSC GENE THERAPY AN...

ORCHARD THERAPEUTICS ANNOUNCES AGREEMENT WITH THE BENELUXA CONSORTIUM ENABLING REIMBURSED ACCESS TO LIBMELDY

25-01-2024
BOSTON AND LONDON, JAN. 25, 2024 (GLOBE NEWSWIRE) -- ORCHARD THERAPEUTICS, A GLOBAL GENE THERAPY LEA...

KYOWA KIRIN SUCCESSFULLY COMPLETES ACQUISITION OF ORCHARD THERAPEUTICS, A GLOBAL GENE THERAPY LEADER FOR RARE DISEASES

24-01-2024
TOKYO & LONDON & BOSTON--(BUSINESS WIRE)--KYOWA KIRIN CO., LTD. (KYOWA KIRIN, TSE: 4151) A JAPAN-BAS...

KYOWA KIRIN SUCCESSFULLY COMPLETES ACQUISITION OF ORCHARD THERAPEUTICS, A GLOBAL GENE THERAPY LEADER FOR RARE DISEASES

24-01-2024
TOKYO AND LONDON AND BOSTON, JAN. 24, 2024 (GLOBE NEWSWIRE) -- KYOWA KIRIN CO., LTD. (KYOWA KIRIN, T...

ORCHARD THERAPEUTICS RECEIVES SWISSMEDIC APPROVAL FOR LIBMELDY IN EARLY-ONSET MLD

11-12-2023
BOSTON AND LONDON, DEC. 11, 2023 (GLOBE NEWSWIRE) -- ORCHARD THERAPEUTICS (NASDAQ: ORTX), A GLOBAL G...

ORCHARD THERAPEUTICS RECEIVES U.S. FDA FAST TRACK DESIGNATION FOR OTL-203 IN MPS-IH

30-11-2023
PREVIOUSLY REPORTED RESULTS FROM ONGOING PROOF-OF-CONCEPT STUDY SHOWED EXTENSIVE METABOLIC CORRECTIO...

ORCHARD THERAPEUTICS INVESTOR ALERT BY THE FORMER ATTORNEY GENERAL OF LOUISIANA: KAHN SWICK & FOTI, LLC INVESTIGATES ADEQUACY OF PRICE AND PROCESS IN PROPOSED SALE OF ORCHARD THERAPEUTICS PLC - ORTX

28-11-2023
NEW ORLEANS--(BUSINESS WIRE)--FORMER ATTORNEY GENERAL OF LOUISIANA CHARLES C. FOTI, JR., ESQ. AND TH...

ORCHARD THERAPEUTICS REPORTS THIRD QUARTER 2023 FINANCIAL RESULTS AND HIGHLIGHTS RECENT BUSINESS ACCOMPLISHMENTS

13-11-2023
REPORTED $5.6 MILLION IN QUARTERLY LIBMELDY NET REVENUE AND $12.7 MILLION YEAR-TO-DATE PLANNED ACQUI...

ORCHARD THERAPEUTICS ANNOUNCES PRESENTATION OF ADDITIONAL POSITIVE DATA FROM PROOF-OF-CONCEPT STUDY OF OTL-203 IN MPS-IH AT ESGCT 2023

26-10-2023
NEW CLINICAL DATA BEYOND PREVIOUSLY REPORTED NEUROLOGICAL AND SKELETAL RESULTS DEMONSTRATE FAVORABLE...

ORCHARD THERAPEUTICS ANNOUNCES MULTIPLE PRESENTATIONS AT ESGCT 2023

24-10-2023
EIGHT PRESENTATIONS HIGHLIGHT THE DIFFERENTIATED PROFILE AND BROAD APPLICABILITY OF THE COMPANY'S HS...

ORCHARD THERAPEUTICS INVESTOR ALERT BY THE FORMER ATTORNEY GENERAL OF LOUISIANA: KAHN SWICK & FOTI, LLC INVESTIGATES ADEQUACY OF PRICE AND PROCESS IN PROPOSED SALE OF ORCHARD THERAPEUTICS PLC - ORTX

06-10-2023
NEW ORLEANS--(BUSINESS WIRE)--FORMER ATTORNEY GENERAL OF LOUISIANA CHARLES C. FOTI, JR., ESQ. AND TH...

ORTX STOCK ALERT: HALPER SADEH LLC IS INVESTIGATING WHETHER THE SALE OF ORCHARD THERAPEUTICS PLC IS FAIR TO SHAREHOLDERS

05-10-2023
NEW YORK--(BUSINESS WIRE)--HALPER SADEH LLC, AN INVESTOR RIGHTS LAW FIRM, IS INVESTIGATING WHETHER T...

KYOWA KIRIN TO ACQUIRE ORCHARD THERAPEUTICS

05-10-2023
-ORCHARD THERAPEUTICS IS A GLOBAL GENE THERAPY LEADER WITH EXPERIENCE SUCCESSFULLY DEVELOPING AND CO...

ORCHARD THERAPEUTICS ANNOUNCES ACCEPTANCE OF BIOLOGICS LICENSE APPLICATION FOR OTL-200 IN MLD AND RECEIVES PRIORITY REVIEW

18-09-2023
PDUFA DATE SET FOR MARCH 18, 2024 OTL-200 WOULD BE THE FIRST AND ONLY TREATMENT IN THE U.S. FOR EARL...

ORCHARD THERAPEUTICS ANNOUNCES PRESENTATION OF DATA COMPRISING THE CLINICAL PACKAGE FOR THE OTL-200 BLA IN MLD AT THE SSIEM ANNUAL SYMPOSIUM 2023

31-08-2023
ADMINISTRATION OF ONE-TIME GENE THERAPY RESULTED IN STATISTICALLY SIGNIFICANT IMPROVEMENT IN SEVERE ...

ORCHARD THERAPEUTICS COMPLETES SUBMISSION OF BIOLOGICS LICENSE APPLICATION FOR OTL-200 IN MLD TO U.S. FDA

03-08-2023
REPORTED $6.6M IN Q2'23 LIBMELDY NET SALES, REPRESENTING THE HIGHEST QUARTER TO DATE $34.0M OF ADDIT...

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